Patients And Families

The needs of patients who suffer from unserved or under-served rare diseases drive our mission at Aceragen.

Our goals

We seek to understand the unique experiences of patients, families, and physicians to guide our development programs.
We aim to be a source of information and resources for individuals and families living with rare disease as well as the physicians and others involved in their care.
We work to increase awareness and understanding of these rare diseases through education and outreach.
We strive to develop novel therapies which can have a positive impact on the lives of patients and families.

Patient Engagement at Aceragen is dedicated to maintaining the patient perspective at the center of our work. We collaborate with patients, caregivers, healthcare providers, and patient organizations to be the bridge between the company and the patient communities we serve.

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